玛乔丽·勃隆夫曼奖学金资助产生了一种携带人类 DUX4 D4Z4 的新型转基因小鼠模型,推进了临床试验准备工作

Research project initiated in 2003 under a FSH Society Marjorie  Bronfman Fellowship Grant yields a new transgenic mouse model with Human DUX4 D4Z4 advancing clinical trials  readiness efforts and our understanding of FSHD   Press Release at PRWeb. Publication online at  PLOS  Genetics

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