Search results for ‘fshd’

Race for a cure!

Race for a cure!

[…] on a jumbotron to some 500,000 fans in attendance. The PSA features eye-catching portraits of FSHD patients and families and encourages fans to donate in support of finding a cure […]

new, improved CRISPR-Cas9 technology

A new, improved CRISPR-Cas9 technology

[…] cells in culture to reverse genetic mutations underlying sickle cell disease and Tay-Sachs disease. For FSHD, prime editing technology has the potential to target and disable the poly-adenylation signal associated […]

Join Us

Join Us

Be part of the movement powering the path forward for people living with FSHD. Whether you’re looking for the latest updates or want to get more involved, we’re here to […]