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[…] its first-in-human clinical trial of EPI-321, a potential first-in-class treatment for facioscapulohumeral muscular dystrophy ( FSHD). The exploratory first-in-human global trial, recently cleared to begin in the United States and […]
[…] turned DUX4 “on”, while in the one on the left, the DUX4 gene remained “off”. FSHD mice have a slow and unsteady gait caused by weakened muscles. You may also […]
Team FSHD Cycling, formed by George Pollock Jr., will participate in the Open Division as an 8 person team in this year’s Race Across America, one of the most respected and longest running ultra-endurance […]
The program agendas for our FSHD Connect conferences are now available to download. Please click on the links provided below. We thank our generous sponsors for their support! FSHD Research […]
Important paper on FSHD published in Human Molecular Genetics by scientists at the BBRI NIH NICHD Sen. Paul Wellstone MDCRC for FSHD. The distinct message in the paper is that DUX4-fl expression is necessary […]
