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[…] structure of the DUX4 protein, which is responsible for the disease, facioscapulohumeral muscular dystrophy ( FSHD). Unlike the majority of genetic diseases, FSHD is not caused by a protein that […]
[…] locally acting “Myostatin+” muscle agent, for the treatment of patients with facioscapulohumeral muscular dystrophy ( FSHD). “We are pleased to receive orphan drug designation for ACE-083, which has shown the […]
[…] annual San Francisco Concert and Conference, given in memory of Joyce Hakansson. Don’t miss our FSHD Family Day Conference and Songs in the Key of Steven Blier benefit concert on Saturday, July 15, […]
[…] keys to success in such a high-pressure job, observations about the game—as well as his FSHD journey. How did he learn he has FSHD, and why did he choose to […]
by William Saraille, Washington DC We hope we that in the not-too-distant future, treatments for FSHD will be approved by the Food and Drug Administration. But when that time comes, […]
