Browsing “2021 - FSHD Society - Page 9”

Angela Lek, PhD, comments on new, improved CRISPR-Cas9 technology

A researcher’s journey into FSHD

  In this FSHD University Webinar from April 15, 2021, Angela Lek, PhD, a research scientist at Yale University School of Medicine, speaks about how her husband’s diagnosis with limb-girdle […]

Pivot

by Larry Chase Those of us who live with FSHD must “pivot” our world constantly. Pivot—the buzz word for what we all are going through and continue to experience, just […]

Arrowhead Pharmaceuticals announces FSHD drug candidate

Arrowhead Pharmaceuticals, Inc., a Pasadena, California, company, today announced ARO-DUX4 as Arrowhead’s first muscle targeted investigational RNAi therapeutic candidate. Using the company’s proprietary Targeted RNAi Molecule (TRIMTM) platform, ARO-DUX4 is […]