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[…] Presentations and breakout sessions slides can be downloaded by clicking on the highlighted titles* below: FSHD Science 101. Alexandra Belayew, PhDÂ (VIDEO) Genetics and genetic testing. Silvere van der Maarel, PhD […]
[…] has granted Orphan Drug Designation to EPI-321 for the treatment of facioscapulohumeral muscular dystrophy ( FSHD), the most common form of muscular dystrophy in adults. EPI-321 is an investigational therapy […]
[…] novel therapies targeting muscle and cardiac tissue. Among the disease KateTx plans to tackle are FSHD and myotonic dystrophy Type 1. Efforts to deliver gene therapies into cells typically rely […]
[…] Gala This year, for the first time, we have combined our two signature meetings into FSHD Connect, a single, three-day super-conference. Our events begin on November 10-11 with Research Connect […]
FSHD research teams in Seattle, Rochester and Leiden add to the existing FSHD model loss of heterochromatin at D4Z4 and the presence of a specific haplotype on chromosome 4 […]
