We are honored that you chose to support us. FSH muscular dystrophy, a debilitating disease affecting nearly a million men, women, and children worldwide, has long lacked any treatment, but because of you, our families can look forward to having a therapy by the year 2025, if not sooner.
Because of you, thousands of families can get support from local chapter leaders and become activists in their communities.
You have catalyzed breakthrough research on stem cells, CRISPR, new treatment strategies, and more than $100 million of private investment in FSHD therapies.
Thanks to you, we are launching the FSHD Therapeutic Accelerator Project to remove barriers to FDA approval of promising treatments.
Together, we have journeyed incredible distances. With your continued support, we will reach our goal!
Mark Stone, President & CEO
Here is our Annual Report Card. Click on the image to enlarge.