[…] the US, Canada, UK, and Europe, there are roughly 2,500 patients. But only about 10 percent – or 250 – of these patients might meet the inclusion criteria for a […]
The challenges of the new era
European FSHD patients speak out
[…] important for any treatment to target. These are: Stopping the progression of the disease – 100% of all respondents wanted this Regaining strength – over 50% of respondents said this […]
(Cautious) optimism in FSHD drug development
[…] hurdles for successfully completing clinical trials is recruiting enough patients to participate in a reasonable period of time. This is exceptionally challenging for a rare disease like FSHD, compared to […]
Good times! TD Garden Tournament
[…] won the playoffs, while Mouse Specifics claimed the Youth team trophy. Following the tournament, around 100 revelers crowded into Causeway Restaurant and Bar for delicious food, plenty of beer and […]
Project 2025
[…] than anyone else’s at Illinois at the time,” Ryan explained. Ryan joined the lab and persuaded Jones to take a look at the disease that had upended his life. The […]